Delandistrogene moxeparvovec is the first gene-replacement therapy for Duchenne muscular dystrophy (DMD) and requires careful patient selection and structured monitoring. Ambulation, defined ...
Correspondence to Dr Sebastian Jason Gray, Paediatric Department, Salisbury District Hospital, Salisbury, SP2 8BJ, UK; Sebastian.Gray{at}Salisbury.nhs.uk Safety netting has likely always occurred but ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results