LONG before finding fame on The Only Way Is Essex, Kelsey Stratford’s life changed forever when she became a carer for her ...

Intrathecal onasemnogene abeparvovec improved HFMSE scores in patients with SMA type 2, indicating enhanced motor function. The STEER study confirmed the therapy's favorable safety profile, with ...

SMA Type 1 is a severe genetic disorder affecting muscle strength and mobility. Former Little Mix star Jesy Nelson reveals ...

Singer Jesy Nelson has opened up sharing that her twin daughters have been diagnosed with Spinal Muscular Atrophy, but what ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Topline results from a phase 3 clinical trial showed an ...

In a multidisciplinary follow-up study, researchers analyzed bone health decline and the effects of nusinersen in patients with spinal muscular atrophy (SMA) types 2 and 3. SMA is a progressive, ...

"Decreasing AMMO [active maximal mouth opening] over time is seen most often in patients with SMA type 2 with an estimated reduction of almost 1 mm per year...At this point, we propose that ...

The singer shared an emotional update about her twins’ health on Sunday and that ‘time is of the essence with this disease’ ...

Former Little Mix star Jesy Nelson revealed on social media that her twin girls have been diagnosed with a rare genetic condition called Spinal Muscular Atrophy (SMA) and may never be able to walk.

Some patients with later-onset spinal muscular atrophy (SMA) type 2 and type 3 had improved motor function when the investigational monoclonal antibody apitegromab was added to their treatment, the ...

SMA type 3 is a hereditary disease that affects motor neurons. People may also refer to it as Kugelberg-Welander disease. Symptoms usually begin after 18 months of age. Children with SMA type 3 can ...