More quality-adjusted life-years with gene therapy, but at a much higher cost ...

Most inborn errors of immunity (IEIs) are caused by defects that arise somewhere along the developmental path between hematopoietic stem cells (HSCs) and mature immune cells. Replacement of mutant ...

For people living with multiple sclerosis (MS), the search for effective treatment options can feel like a never-ending journey. While disease-modifying therapies (DMTs) have improved outcomes for ...

A collaborative team of researchers from Children's Hospital of Philadelphia (CHOP) found that hematopoietic stem cell transplantation (HSCT) is a highly effective method for treating patients with ...

UM171 Cell Therapy is conditionally approved in Europe as Zemcelpro® (dorocubicel)Securing Canadian rights to a proprietary ...

One of the greatest medical success stories in recent years is the successful treatment of acute leukemia in children. Just a few decades ago, mortality was universal. Now, survival has improved to ...

Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease symptoms and low rates of severe side effects or complications years after ...

How does a bone marrow transplant work? Answer: There are really two forms of hematopoietic stem cell transplants, commonly known as bone marrow transplants. An autologous transplant is typically used ...

Stem cell treatments are being sold abroad for ALS, sports injuries and more. Here’s what the FDA has actually approved.